September 2020 (tbc) – Gene Therapy Webinar
If you are interested in learning about gene therapies, and hearing about the latest developments for Inherited Metabolic Disorders, join us at our live webinar. For more information click here
10th & 11th October 2020 – Annual Conference
Our 38th annual conference, Patient Participation: Creating Patient Leaders, will this year take place online for the first time! Register your place and discover more about our conference here.
What does early access actually mean? (recorded 15.07.2020)
Click here to watch our webinar with Bionical Emas and FindaCure on what early access programmes are and how patient groups can engage with them.